Using just two fingers, a 23-year-old Hong Kong woman who is almost completely paralysed by a rare disease has written a proposal calling for patients to be treated with a new drug that could be life-saving.
Josy Chow Pui-shan, who was born with spinal muscular atrophy (SMA), a genetic disorder that gradually destroys physical abilities such as walking and breathing, urged the government to introduce nusinersen, marketed as Spinraza, the first approved drug for SMA by the US Food and Drug...
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